Evidence memo / Reproductive & endocrine

Terlipressin

Also: Terlivaz · Glypressin

Terlipressin (Terlivaz) is a vasopressin analog approved in the US to improve kidney function in adults with hepatorenal syndrome who have a rapid decline in kidney function. It has long been used elsewhere for bleeding from esophageal varices. The approved use is specific and serious. The Watchlist boundary is keeping it to its approved hepatorenal indication and noting its respiratory and ischemic risks.

Approved for specific usesApproved specific useSafety / regulatory watch

The verdict

Our read at a glance.

Whether terlipressin's approved hepatorenal syndrome use is understood within that specific, serious indication and its risk profile, rather than generalized.

The signal
Randomized trials, including the CONFIRM trial, support terlipressin for improving kidney function in hepatorenal syndrome, though the benefit comes with notable risks. It also has a long international track record in variceal bleeding.
The unknown
How to weigh its kidney benefit against serious risks such as respiratory failure, and which patients are most likely to benefit safely.
Our read
A serious hospital drug for a life-threatening condition, with real benefit and real risk. Terlipressin can improve kidney function in hepatorenal syndrome, but its respiratory and ischemic warnings mean it belongs only in that specific, supervised setting.

The mechanism

How it works.

Terlipressin is a synthetic analog of vasopressin (a prodrug slowly converted to lysine-vasopressin in the body) that activates V1 receptors on smooth muscle in blood vessels, making them constrict. It works mainly in the splanchnic circulation supplying the gut, and squeezing those vessels raises blood pressure in the rest of the body so more blood reaches the kidneys in hepatorenal syndrome. In variceal bleeding, the same constriction cuts blood flow and pressure in the dilated veins that are bleeding.

Safety & regulatory boundary

The consequential part.

Terlipressin carries a boxed warning for serious or fatal respiratory failure and is not recommended in patients with certain levels of kidney dysfunction or in advanced acute-on-chronic liver failure, and it can cause ischemic events. It is a hospital-administered drug for a specific serious indication. Terlivaz and other terlipressin products are not the same as compounded or research-labeled terlipressin, and the approved use does not extend to any general or wellness setting.

What's next

What we're watching.

Real-world safety in hepatorenal syndrome, patient-selection refinements, and comparative data with other vasoconstrictor strategies.

Context

Why this is discussed.

Terlipressin addresses hepatorenal syndrome, a life-threatening kidney complication of advanced liver disease, where options are limited.

The evidence base

21 cited references.

Regulatory & labels1

DailyMed label: Terlivaz

Mallinckrodt Hospital Products Inc. (FDA label) · 2025

Registered trials8

Endothelin Receptor Antagonism With Ambrisentan to Treat Hepatorenal Syndrome

ClinicalTrials.gov · PHASE2 · ACTIVE_NOT_RECRUITING · 2024-04-17

Albumin in Acute Variceal Bleeding

ClinicalTrials.gov · PHASE3 · NOT_YET_RECRUITING · 2026-03-01

Keep reading

Related published memos.